Clinical trial NCT04478981 - References

SELENON-related Myopathy — The Natural History of Patients With Mutations in SEPN1 (SELENON) or LAMA2

Citation(s)

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The Natural History of Patients With Congenital Muscular Dystrophies Due to Mutations in the SELENON or LAMA2 Genes: Working Towards Trial-readiness in Two Mitochondrial Myopathy Mimics

Details for clinical trial NCT04478981