Duchenne Muscular Dystrophy (DMD) — A Study to Evaluate the Safety and Tolerability of GEN6050X in Duchenne Muscular Dystrophy.
Citation(s)
A Single-arm, Open-label, Single-center Study to Evaluate the Safety and Tolerability of Intravenous GEN6050X Gene Therapy in Ambulatory Boys With Duchenne Muscular Dystrophy (DMD).