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A Study to Prospectively Assess Disease Progression in Male Children With X-ALD

X-Linked Adrenoleukodystrophy Clinical Trial

Official title:
A Non-interventional Study to Prospectively Assess Baseline Status and Disease Progression in Male Children With X-Linked Adrenoleukodystrophy

Clinical Trial Summary

This is a non-interventional, multi-center study that follows general principles of periodic assessment of X-ALD patients in routine practice. No study drug treatment will be given and no changes to patient treatment are necessary.

Clinical Trial Description

This is a non-interventional, multi-center study that follows general principles of periodic assessment of X-ALD patients in routine practice. No study drug treatment will be given and no changes to the patient treatment are necessary.

Patients with X-ALD will be recruited and invited to attend a baseline visit. After eligible patients are enrolled, retrospective and baseline data will be collected. After enrollment, patients will be seen approximately every 6 months until they meet withdrawal criteria or the Sponsor terminates the study. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT03278899
Study type Observational
Source NeuroVia, Inc.
Contact Program Director
Phone 415-870-6967
Email patients@neurovia-inc.com
Status Recruiting
Phase
Start date February 16, 2018
Completion date June 1, 2021
View Details
See also
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