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A Phase I/II Study of VTX-801 in Adult Patients With Wilson's Disease — GATEWAY  

Wilson's Disease Clinical Trial

Official title:
A Phase I/II, Multicenter, Non-randomized, Open Label, Adaptive Design, 5-year Follow-up, Single Dose-escalation Study of VTX-801 in Adult Patients With Wilson's Disease

Clinical Trial Summary

The objectives of this clinical trial are to assess, for up to 5 years, the safety, tolerability and pharmacological activity of a single ascending doses of VTX-801, a gene therapy, administered intravenously (IV) to adult patients with Wilson's Disease prior to and following background WD therapy withdrawal.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04537377
Study type Interventional
Source Vivet Therapeutics SAS
Contact Sonia Valero
Phone +33 1 83 81 17 10
Email info@vivet-therapeutics.com
Status Recruiting
Phase Phase 1/Phase 2
Start date September 3, 2021
Completion date March 2029
View Details
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