Prospective Study of the Natural History of Patients With Type 2 and 3 Spinal Muscular Atrophy — NatHis-SMA  

Type 2 Spinal Muscular Atrophy Clinical Trial

Official title: Prospective Study of the Natural History of Patients With Type 2 and 3 Spinal Muscular Atrophy

Status Completed

Clinical Trial Summary

NatHis-SMA is a prospective, longitudinal and interventional study of the natural history of patients with type 2 and 3 Spinal Muscular Atrophy (SMA). The purpose of this study is to characterize the disease course over 2 years and identify prognostic variables of the disease and biomarkers of SMA progression, as well as determine the best outcome measures for further therapeutics approaches.

Clinical Trial Description

n/a

Related Conditions & MeSH terms

• Atrophy
• Muscular Atrophy
• Muscular Atrophy, Spinal
• Type 2 Spinal Muscular Atrophy
• Type 3 Spinal Muscular Atrophy

• NCT number: NCT02391831
• Study type: Interventional
• Source: Institut de Myologie, France
• Status: Completed
• Phase: N/A
• Start date: May 2015
• Completion date: June 2018