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Sun May Arise on SMA : Newborn Screening of Spinal Muscular Atrophy in Belgium

Spinal Muscular Atrophy Clinical Trial

Official title:
Sun May Arise on SMA : Newborn Screening of SMA in Belgium

Clinical Trial Summary

Medico-economic study of Newborn screening of Spinal Muscular Atrophy

Clinical Trial Description

The aim of this project is to demonstrate the feasibility and the medico-economic impact of a spinal muscular atrophy neonatal screening in a European country. We propose a 3-year-neonatal screening program in Southern Belgium (Wallonia-Brussels Federation) where there is 59.000 newborns/year, among whom 6 are affected by spinal muscular atrophy. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT03554343
Study type Observational
Source Centre Hospitalier Régional de la Citadelle
Contact
Status Completed
Phase
Start date March 5, 2018
Completion date February 28, 2021
View Details
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