European Registry of Patients With Infantile-onset Spinal Muscular Atrophy

See also
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Recruiting	`NCT05779956` - Personalized Medicine for SMA: a Translational Project
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Completed	`NCT01703988` - An Open-label Safety, Tolerability and Dose-Range Finding Study of Multiple Doses of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy	Phase 1/Phase 2
Withdrawn	`NCT02235090` - Study of Feasibility to Reliably Measure Functional Abilities' Changes in Nonambulant Neuromuscular Patients Without Trial Site Visiting	N/A
Completed	`NCT02123186` - Newborn Screening for Spinal Muscular Atrophy	N/A
Completed	`NCT00756821` - A Pilot Study of Biomarkers for Spinal Muscular Atrophy	N/A
Completed	`NCT00004771` - Phase II Study of Leuprolide and Testosterone for Men With Kennedy's Disease or Other Motor Neuron Disease	Phase 2
Recruiting	`NCT05366465` - Quality of Life and Participation of the Adult With Spinal Muscular Atrophy in France
Recruiting	`NCT06310421` - Spinal Muscular Atrophy Neonatal Screening Program

NCT number	NCT03339830
Study type	Observational [Patient Registry]
Source	Institut de Myologie, France
Contact
Status	Completed
Phase
Start date	October 10, 2017
Completion date	November 15, 2020

European Registry of Patients With Infantile-onset Spinal Muscular Atrophy

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms