Pyruvate Kinase Deficiency Clinical Trial
Official title:
An Open-Label, Multicenter, Extension Study of AG-348 in Adult Subjects With Pyruvate Kinase Deficiency Previously Enrolled in AG-348 Studies
This is a multicenter, open-label, extension study to evaluate the long-term safety, tolerability, and efficacy of treatment with AG-348 in participants who were previously enrolled in Study AG348-C-006 or Study AG348-C-007.
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Status | Clinical Trial | Phase | |
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Completed |
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Completed |
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Not yet recruiting |
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