Pompe Disease Clinical Trial
Official title:
Electrical Impedance Myography and Muscle Ultrasound: Longitudinal Measures in Pompe Disease
Study Objectives:
1. Determine the correlation between quantitative muscle ultrasound (QMUS), electrical
impedance myography (EIM) and currently accepted measures of physical function.
2. Determine the reliability of EIM measures performed in the home through use of a hand
held device.
3. Determine if QMUS and EIM can detect pre-clinical changes in Pompe disease.
n/a
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