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Clinical Trial Summary

The goals of this study are to determine safety and efficacy with regard to motor function of oral clenbuterol in combination with ERT in subjects with LOPD


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT04094948
Study type Interventional
Source Duke University
Contact
Status Withdrawn
Phase Phase 2
Start date January 1, 2023
Completion date December 30, 2025

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