Pompe Disease (Late-onset) Clinical Trial
Official title:
Phase II Clinical Trial of Clenbuterol in Adult Patients With Pompe Disease Stably Treated With Enzyme Replacement Therapy
The goals of this study are to determine safety and efficacy with regard to motor function of oral clenbuterol in combination with ERT in subjects with LOPD
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Status | Clinical Trial | Phase | |
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Completed |
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Phase 3 | |
Recruiting |
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Phase 1/Phase 2 | |
Active, not recruiting |
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Phase 1/Phase 2 | |
Completed |
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Recruiting |
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MSOT in Pompe Disease
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N/A | |
Recruiting |
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Pompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease
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Active, not recruiting |
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Developing a Management Approach for Patients With "Late-Onset" Pompe Disease
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Completed |
NCT00731081 -
Study About the Evolution of Severe Late Onset Pompe Disease Patient With Pulmonary Dysfunction and Receiving Myozyme®
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N/A | |
Completed |
NCT00455195 -
Late-Onset Treatment Study Extension Protocol
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Phase 4 | |
Recruiting |
NCT05951790 -
Inspiratory Muscle Training (IMT) in Adult People With Pompe Disease
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N/A | |
Completed |
NCT01288027 -
Exploratory Muscle Biopsy Assessment Study in Patients With Late-Onset Pompe Disease Treated With Alglucosidase Alfa
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Phase 4 | |
Recruiting |
NCT00567073 -
Pompe Pregnancy Sub-Registry
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Completed |
NCT03893240 -
Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease
|
N/A | |
Completed |
NCT00250939 -
A Study of rhGAA in Patients With Late-Onset Pompe Disease
|
Phase 2 | |
Recruiting |
NCT03911505 -
ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPD
|
Phase 3 | |
Recruiting |
NCT06150820 -
A Study About Antibody Levels and Biomarkers in the Blood in People With Late-onset Pompe Disease
|
N/A | |
Completed |
NCT03729362 -
A Study Comparing ATB200/AT2221 With Alglucosidase Alfa/Placebo in Adult Subjects With Late-onset Pompe Disease
|
Phase 3 | |
Not yet recruiting |
NCT06178432 -
Evaluation of the Safety, Tolerability and Efficacy of Gene Therapy Drug for Late Onset Pompe Disease (LOPD)
|
Early Phase 1 | |
Completed |
NCT00268944 -
Safety and Effectiveness Study of rhGAA in Patients With Advanced Late-Onset Pompe Disease Receiving Respiratory Support
|
Phase 3 | |
Active, not recruiting |
NCT04138277 -
A Study to Assess the Long-term Safety and Efficacy of ATB200/AT2221 in Adult Subjects With LOPD
|
Phase 3 |