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Clinical Trial Summary

The main purpose of this study is to evaluate the long-term safety of PTC923 in participants with phenylketonuria, and to evaluate the changes from baseline in dietary phenylalanine (Phe)/protein consumption.


Clinical Trial Description

Eligible participants are: Feeder participants: those who have completed a Phase 3 PTC Therapeutics (PTC) sponsored feeder study (including Study PTC923-MD-003-PKU). Non-feeder controlled participants: those who have not completed a feeder study and have blood Phe levels <360 μmol/L at study entry. Non-feeder uncontrolled participants: those who have not completed a feeder study and have blood Phe levels ≥360 μmol/L at study entry. ;


Study Design


Related Conditions & MeSH terms


NCT number NCT05166161
Study type Interventional
Source PTC Therapeutics
Contact Patient Advocacy
Phone 1-866-562-4620
Email medinfo@ptcbio.com
Status Recruiting
Phase Phase 3
Start date February 14, 2022
Completion date February 7, 2025

See also
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