Long-Term Follow Up Study of Subjects Previously Administered HMI 102

Status Enrolling by invitation

Clinical Trial Summary

An Open-Label, Long-Term Follow Up Study of Safety and Efficacy in PKU Subjects with PAH Deficiency Previously Administered HMI 102

Clinical Trial Description

This Long-Term Follow Up Study will evaluate the safety and efficacy of PKU Subjects with PAH Deficiency Previously Administered HMI 102. Subjects will have already received a single dose of HMI-102 administered intravenously ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT04348708
Study type	Observational
Source	Homology Medicines, Inc
Contact
Status	Enrolling by invitation
Phase
Start date	August 19, 2020
Completion date	December 1, 2026

View Details

See also
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