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Kuvan®'s Effect on the Cognition of Children With Phenylketonuria — KOGNITO  

Phenylketonuria Clinical Trial

Official title:
A Phase 4 Open-Label, Single-Cohort Study of the Long-Term Neurocognitive Outcomes in 4 to 5 Year-Old Children With Phenylketonuria Treated With Sapropterin Dihydrochloride (Kuvan®) for 7 Years

Clinical Trial Summary

The study is a single-cohort, interventional, open-label trial to evaluate long-term neurocognitive (NC) outcomes in children aged 4 to 5 years with phenylketonuria (PKU) treated with Kuvan® and Phenylalanine-restricted diet over a period of 7 years.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT01965912
Study type Interventional
Source BioMarin Pharmaceutical
Contact
Status Completed
Phase Phase 4
Start date October 2013
Completion date January 4, 2023
View Details
See also
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