Neuronal Ceroid-Lipofuscinoses Clinical Trial
Official title:
A Study in Subjects With Neuronal Ceroid Lipofuscinoses Taking Trehalose
Neuronal Ceroid Lipofuscinoses (NCL) or Batten's disease are the most common juvenile neurodegenerative disease, characterized by early blindness, movement disorders, cognitive and behavioral impairment, epilepsy, and retinopathy. This study aims to collect clinical and laboratory data of patients with NCL taking Trehalose.
This study aims to collect clinical and laboratory data of patients with NCL taking Trehalose. ;
Status | Clinical Trial | Phase | |
---|---|---|---|
Active, not recruiting |
NCT04098211 -
Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients
|
||
Enrolling by invitation |
NCT03862274 -
Examining Developmental Outcomes of Children Diagnosed With CLN2 Disease
|