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Clinical Trial Summary

The TOPAZ study will assess the safety and efficacy of SRK-015 in later-onset Spinal Muscular Atrophy (SMA Type 2 and Type 3) in pediatric and adult patients.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT03921528
Study type Interventional
Source Scholar Rock, Inc.
Contact
Status Completed
Phase Phase 2
Start date April 22, 2019
Completion date February 28, 2024

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