Mucopolysaccharidosis II Clinical Trial
Official title:
Phase II Study of JR-141 in Patients With Mucopolysaccharidosis II
A Phase II open-label, randomized, parallel group, 2 sites (Brazil), designed to evaluate the safety and efficacy of 3 doses of study drug for the treatment of the MPS II.
n/a
| Status | Clinical Trial | Phase | |
|---|---|---|---|
| Withdrawn |
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Phase 2/Phase 3 | |
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Phase 1 | |
| Completed |
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Phase 2/Phase 3 | |
| Completed |
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| Completed |
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Phase 1/Phase 2 | |
| Active, not recruiting |
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| Terminated |
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Phase 2/Phase 3 | |
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| Completed |
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Phase 1/Phase 2 | |
| Terminated |
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Phase 1/Phase 2 | |
| Enrolling by invitation |
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| Completed |
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Phase 1/Phase 2 | |
| Withdrawn |
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| Enrolling by invitation |
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