Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02

MPS VI Clinical Trial

Official title:
A Re-Survey Study of Patients With MPS VI (Maroteaux-Lamy Syndrome) Who Previously Participated in ASB-00-02

Status Completed

Clinical Trial Summary

There is limited information on the long-term effects of treating patients with MPS VI with Naglazyme® and limited data on the natural history of treated and untreated MPS VI patients. The Re-survey Study ASB-00-03 will assist in understanding the effects of long-term Naglazyme treatment and the natural history of the MPS VI patient population.

Clinical Trial Description

n/a

Study Design

N/A

Related Conditions & MeSH terms

MPS VI

Clinical Trial Details

NCT number	NCT01387854
Study type	Observational
Source	BioMarin Pharmaceutical
Contact
Status	Completed
Phase	N/A
Start date	June 2011
Completion date	February 2013

View Details

See also
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Active, not recruiting	`NCT03632213` - Evaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI	Phase 2
Recruiting	`NCT04532047` - In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases	Phase 1