Mitochondrial Diseases Clinical Trial
Official title:
An Open-Label Dose-Escalation Phase I Study to Asses the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of RG2133 (2',3',5'-Tri-O-Acetyluridine) in the Treatment of Inherited Mitochondrial Diseases
The objective of the study is to determine the safety and tolerability of RG2133 in patients with Mitochondrial Disease.
n/a
Allocation: Non-Randomized, Primary Purpose: Treatment
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