Weekly Sirolimus Therapy

Status Recruiting

Clinical Trial Summary

In current practice, options for venous and lymphatic malformations remain limited. Recently an oral medication, sirolimus, has been found to benefit patients when taken once or twice a day for several months. Unfortunately there are many side effects associated with this medication, some of which can be severe including, neutropenia, oral ulcerations, and lab abnormalities. The purpose of this study is to determine if once weekly dosed sirolimus will be effective for the treatment of venous and lymphatic malformations. Additionally, the study will evaluate patient satisfaction and identify adverse effects. Participants will be on the medication for 6 months with an option to continue after this time period.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT04861064
Study type	Interventional
Source	Medical University of South Carolina
Contact	Stephnie Munie, BS
Phone	843-566-2453
Email	munie@musc.edu
Status	Recruiting
Phase	Phase 2
Start date	January 18, 2022
Completion date	June 2025

View Details

See also
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