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Leber Congenital Amaurosis (LCA) clinical trials

View clinical trials related to Leber Congenital Amaurosis (LCA).

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NCT ID: NCT02946879 Completed - Eye Diseases Clinical Trials

Long-Term Follow-Up Gene Therapy Study for Leber Congenital Amaurosis OPTIRPE65 (Retinal Dystrophy Associated With Defects in RPE65)

Start date: November 2016
Phase:
Study type: Observational

This study is a longer-term follow-up study for patients who have been administered AAV2/5-OPTIRPE65 in the Phase I/II, open label, non-randomised, two-centre, dose escalation trial in adults and children with retinal dystrophy associated with defects in RPE65.

NCT ID: NCT02575430 Completed - Clinical trials for Retinitis Pigmentosa (RP)

Natural History Study in Inherited Retinal Disease Subjects Caused by Mutations in RPE65 or LRAT

Start date: December 2015
Phase: N/A
Study type: Observational

To evaluate the natural history of visual function in subjects with IRD phenotypically diagnosed as Leber congenital amaurosis (LCA) or retinitis pigmentosa (RP) caused by RPE65 or LRAT gene mutations.