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Induced Pluripotent Stem Cells for the Development of Novel Drug Therapies for Inborn Errors of Metabolism (iPSC-IEM) — iPSC-IEM  

Inborn Errors of Metabolism Clinical Trial

Official title:
Induced Pluripotent Stem Cells for the Development of Novel Drug Therapies for Inborn Errors of Metabolism, an International, Multicenter Study

Clinical Trial Summary

Human induced pluripotent stem cells (iPSCs), are reprogrammed from somatic cells that can self-renew indefinitely and produce different types of cells. They provide human model cell lines for orphan drug development. It is the goal of this study to define new cellular disease models for Inborn Erors of Metabolism, as enabling tools for both drug discovery and development.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04097275
Study type Observational
Source CENTOGENE GmbH Rostock
Contact Peter Bauer, Prof.
Phone +49 30767584871
Email Peter.Bauer@centogene.com
Status Recruiting
Phase
Start date August 1, 2019
Completion date August 1, 2024
View Details
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