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Post Marketing Surveillance (PMS) Study for Velaglucerase Alfa (VPRIV) in India

Gaucher Disease Clinical Trial

Official title:
A Post Marketing Surveillance (PMS) Study for VPRIV (Velaglucerase Alfa) in India

Clinical Trial Summary

The main aim of this study is to measure the safety and to find out the effects of VPRIV in participants with Gaucher disease using both retrospective and prospective data when used in the post-marketing setting and to collect genetic mutation data from participants with Gaucher disease. This study is about collecting data available in the participant's medical record as well as data from each participant's ongoing treatment. No study medicines will be provided to participants in this study. When the participants start the study, they will visit the study clinic close to approximately 12 months.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04429984
Study type Observational
Source Takeda
Contact
Status Completed
Phase
Start date July 28, 2021
Completion date April 22, 2023
View Details
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