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Miglustat on Gaucher Disease Type IIIB

Gaucher Disease Clinical Trial

Official title:
Evaluation of Combination Therapy With Miglustat and Enzyme Replacement Therapy on Gaucher Disease Type IIIB

Clinical Trial Summary

evaluate the combination therapy with Miglustat and enzyme replacement therapy (ERT) on Gaucher disease

Clinical Trial Description

understand if Miglustat (glucosylceramide synthase inhibitor) could improve neuropathy in patients with Gaucher disease ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT02520934
Study type Interventional
Source National Taiwan University Hospital
Contact
Status Active, not recruiting
Phase N/A
Start date July 2015
Completion date December 2019
View Details
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