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Clinical Trial Summary

A protocol to extend the assessment of the safety and efficacy of taliglucerase alfa in pediatric subjects (2 to <18 years old) with symptoms and clinical manifestations of Gaucher disease who completed treatment in Protocols PB-06-002 (switchover study from imiglucerase) or PB-06-005 (naïve treatment with taliglucerase alfa).


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT01411228
Study type Interventional
Source Pfizer
Contact
Status Completed
Phase Phase 3
Start date September 2011
Completion date August 2014

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