Fabry Disease Clinical Trial
Official title:
Study Based on Electronic Health RecOrds to Identify Patients at High-risk of Fabry DiseasE
Primary objective: To estimate the prevalence of patients who are at high-risk for Fabry Disease (FD) in the Cleveland Clinic, Abu Dhabi (CCAD) United Arab Emirates (EMR) database from May 2016 to May 2022, according to the predictive algorithm (i.e., feasibility assessment eligibility criteria) Secondary objectives: - To estimate the prevalence of FD among patients at high-risk for FD (i.e., among enrolled patients) - To characterize the patient profile, overall and in Cohorts 1 and 2 - To describe the most common characteristics among positive FD patients and negative FD patients
Patients at high-risk for FD will be consecutively enrolled over approximately 6 months ;
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