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Open-Label Expanded Access Treatment With Pegunigalsidase Alfa for Fabry Disease Patients

Fabry Disease Clinical Trial

Official title:
Expanded Access Treatment With Open-Label Pegunigalsidase Alfa for Fabry Patients

Clinical Trial Summary

The objective of this treatment protocol is to provide guidance to Treating Physicians who seek access to pegunigalsidase alfa for Fabry patients whose clinical condition, in the opinion of the Treating Physician, requires treatment with enzyme replacement therapy (ERT) with pegunigalsidase alfa and a) cannot be adequately treated with currently approved FDA products and/or b) are not able or willing to participate in any of the on-going clinical trials in the United States.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04552691
Study type Expanded Access
Source Chiesi Farmaceutici S.p.A.
Contact Medical Information Chiesi
Phone (888) 661-9260
Email us.medical@chiesi.com
Status Available
Phase
View Details
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