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Clinical Trial Summary

Primary Objective:

To assess the safety, pharmacokinetics (PK), pharmacodynamics (PD), and exploratory efficacy of GZ/SAR402671 in enzyme replacement therapy treatment-naïve adult male participants diagnosed with Fabry disease.


Clinical Trial Description

The total duration of study per participant was 7 to 8 months for participants who entered a planned extension study and approximately 13 to 14 months for participants who did not enter a planned extension study. A 2-year extension study was planned for eligible participants. ;


Study Design


Related Conditions & MeSH terms


NCT number NCT02228460
Study type Interventional
Source Sanofi
Contact
Status Completed
Phase Phase 2
Start date November 2014
Completion date September 2016

See also
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