Fabry Disease Clinical Trial
Official title:
A Phase 2 Study to Evaluate the Safety, Pharmacodynamics, Pharmacokinetics, and Exploratory Efficacy of GZ/SAR402671 in Enzyme Replacement Therapy (ERT) Treatment-naïve Adult Male Patients Diagnosed With Fabry Disease
Primary Objective:
To assess the safety, pharmacokinetics (PK), pharmacodynamics (PD), and exploratory efficacy
of GZ/SAR402671 in enzyme replacement therapy treatment-naïve adult male participants
diagnosed with Fabry disease.
The total duration of study per participant was 7 to 8 months for participants who entered a planned extension study and approximately 13 to 14 months for participants who did not enter a planned extension study. A 2-year extension study was planned for eligible participants. ;
| Status | Clinical Trial | Phase | |
|---|---|---|---|
| Recruiting |
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