Erythropoietic Protoporphyria Clinical Trial
OBJECTIVES:
I. Determine the long-term efficacy and safety of L-cysteine in the prevention
photosensitivity in patients with erythropoietic protoporphyria.
Status | Completed |
Enrollment | 50 |
Est. completion date | September 2001 |
Est. primary completion date | |
Accepts healthy volunteers | No |
Gender | Both |
Age group | 18 Years to 65 Years |
Eligibility |
PROTOCOL ENTRY CRITERIA: --Disease Characteristics-- Erythropoietic protoporphyria RBC protoporphyrin greater than 50 micrograms/100 dL --Prior/Concurrent Therapy-- At least 3 months since prior betacarotene or L-cysteine No concurrent betacarotene --Patient Characteristics-- - Fertile female patients must use effective contraception for duration of trial and for 3 weeks thereafter - Not pregnant or nursing |
Primary Purpose: Treatment
Country | Name | City | State |
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n/a |
Lead Sponsor | Collaborator |
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Brigham and Women's Hospital |
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