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Clinical Trial Summary

This is a multicenter, open-label, dose-escalation study to evaluate the safety, tolerability, and PK of once-weekly IV infusions of eteplirsen in approximately 12 male participants, ages 6 months to 48 months (inclusive), who have genotypically confirmed DMD with a deletion mutation amenable to exon 51 skipping.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT03218995
Study type Interventional
Source Sarepta Therapeutics, Inc.
Contact
Status Completed
Phase Phase 2
Start date August 16, 2017
Completion date March 10, 2021

See also
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