APECED Clinical Trial - Evaluation Genotypic, Phenotypic & Prognosis

See also
	Status	Clinical Trial	Phase
	Completed	`NCT01953016` - Participation in a Research Registry for Immune Disorders
	Recruiting	`NCT01386437` - Natural History of Individuals With Immune System Problems That Lead to Fungal Infections
	Not yet recruiting	`NCT04902807` - Conception of a Diagnosis, Prognosis and Therapeutic Decision Tool for Patients With Autoimmunity and Inflammation

See also

Status

Clinical Trial

Phase

Completed

NCT01953016 - Participation in a Research Registry for Immune Disorders

Recruiting

NCT01386437 - Natural History of Individuals With Immune System Problems That Lead to Fungal Infections

Not yet recruiting

NCT04902807 - Conception of a Diagnosis, Prognosis and Therapeutic Decision Tool for Patients With Autoimmunity and Inflammation

Interventional studies are often prospective and are specifically tailored to evaluate direct impacts of treatment or preventive measures on disease.

Observational studies are often retrospective and are used to assess potential causation in exposure-outcome relationships and therefore influence preventive methods.

Expanded access is a means by which manufacturers make investigational new drugs available, under certain circumstances, to treat a patient(s) with a serious disease or condition who cannot participate in a controlled clinical trial.

Clinical trials are conducted in a series of steps, called phases - each phase is designed to answer a separate research question.

Phase 1: Researchers test a new drug or treatment in a small group of people for the first time to evaluate its safety, determine a safe dosage range, and identify side effects.
Phase 2: The drug or treatment is given to a larger group of people to see if it is effective and to further evaluate its safety.
Phase 3: The drug or treatment is given to large groups of people to confirm its effectiveness, monitor side effects, compare it to commonly used treatments, and collect information that will allow the drug or treatment to be used safely.
Phase 4: Studies are done after the drug or treatment has been marketed to gather information on the drug's effect in various populations and any side effects associated with long-term use.

NCT number	NCT03751683
Study type	Observational
Source	University Hospital, Lille
Contact
Status	Active, not recruiting
Phase
Start date	July 30, 2009
Completion date	September 2020

Evaluation Genotypic, Phenotypic and Prognosis APECED Syndrome — APECED

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms