CSL200 Gene Therapy in Adults With Severe Sickle Cell Disease

Status Terminated

Clinical Trial Summary

This is a phase 1 pilot study of CSL200 in adult subjects with severe sickle cell disease. The primary objectives of this study are to evaluate the safety of the following: collection of CD34+ hematopoietic stem / progenitor cells by apheresis after mobilization with plerixafor, reduced intensity conditioning with melphalan, and administration of CSL200.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Anemia, Sickle Cell

Clinical Trial Details

NCT number	NCT04091737
Study type	Interventional
Source	CSL Behring
Contact
Status	Terminated
Phase	Phase 1
Start date	October 2, 2019
Completion date	May 5, 2021

View Details

See also
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