Adenosine Deaminase Deficiency Clinical Trial
Official title:
Phase I Gene Therapy Protocol for Adenosine Deaminase Deficiency
Adenosine deaminase deficiency is an inherited disorder that results in severe abnormalities of the immune system and leaves children unable to fight infection. This trial aims to treat adenosine deaminase deficiency patients using gene therapy.
n/a
Allocation: Non-Randomized, Intervention Model: Single Group Assignment, Masking: Open Label, Primary Purpose: Treatment
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