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Clinical Trial Details — Status: Completed

Administrative data

NCT number NCT01854047
Other study ID # DRI12544
Secondary ID 2013-000856-16U1
Status Completed
Phase Phase 2
First received May 10, 2013
Last updated November 27, 2015
Start date June 2013
Est. completion date April 2015

Study information

Verified date November 2015
Source Sanofi
Contact n/a
Is FDA regulated No
Health authority United States: Food and Drug Administration
Study type Interventional

Clinical Trial Summary

Primary Objective:

To evaluate the efficacy of different doses and regimens of dupilumab in patients with moderate to severe uncontrolled asthma

Secondary Objective:

To evaluate different doses and regimens of dupilumab in patients with moderate to severe uncontrolled asthma, with regard to:

- Safety and tolerability

- Dupilumab systemic exposure and anti-drug antibodies


Description:

Total duration per participant of approximately 43 weeks including a screening period (14-21 days) , a randomized treatment period (24 weeks), and a post-treatment period (16 weeks).


Recruitment information / eligibility

Status Completed
Enrollment 776
Est. completion date April 2015
Est. primary completion date November 2014
Accepts healthy volunteers No
Gender Both
Age group 18 Years and older
Eligibility Inclusion criteria:

Patients with a physician diagnosis of moderate to severe, uncontrolled asthma for =12 months, based on the Global Initiative for Asthma (GINA) 2009 Guidelines and:

- Existing treatment with moderate- or high-dose inhaled corticosteroid / long-acting beta-2 agonist

- Forced expiratory volume (FEV1) 40 to 80% of predicted normal

- Juniper Asthma Control Questionnaire, 5-question version (ACQ-5) score =1.5

- Reversibility of at least 12% and 200 mL in forced expiratory volume (FEV1)

- Has experienced, within prior year: hospitalization, emergency or urgent care visit or systemic corticosteroid treatment for worsening asthma

Exclusion criteria:

- Patients <18 years

- Chronic obstructive pulmonary disease (COPD) or other lung diseases (eg, emphysema, idiopathic pulmonary fibrosis, Churg-Strauss syndrome, allergic bronchopulmonary aspergillosis) which impair pulmonary function tests

- Chest X-ray within 12 months of screening visit or at screening visit with clinically significant findings of lung disease(s) other than asthma

- Current smoker or cessation of smoking within 6 months prior to Visit 1

- Previous smoker with a smoking history >10 pack-years

The above information is not intended to contain all considerations relevant to a patient's potential participation in a clinical trial.

Study Design

Allocation: Randomized, Endpoint Classification: Safety/Efficacy Study, Intervention Model: Parallel Assignment, Masking: Double Blind (Subject, Caregiver, Investigator), Primary Purpose: Treatment


Related Conditions & MeSH terms


Intervention

Drug:
Dupilumab
Pharmaceutical form: solution Route of administration: subcutaneous
placebo
Pharmaceutical form: solution Route of administration: subcutaneous
Inhaled corticosteroid/long-acting beta-2 agonist (ICS/LABA) therapy
Mometasone furoate /formoterol, budesonide / formoterol, or fluticasone propionate / salmeterol at stable dose, oral inhalation

Locations

Country Name City State
Argentina Investigational Site Number 032003 Buenos Aires
Argentina Investigational Site Number 032004 Buenos Aires
Argentina Investigational Site Number 032001 Caba
Argentina Investigational Site Number 032008 Caba
Argentina Investigational Site Number 032010 Caba
Argentina Investigational Site Number 032002 La Plata
Argentina Investigational Site Number 032005 Rosario
Argentina Investigational Site Number 032006 Rosario
Argentina Investigational Site Number 032007 Rosario
Argentina Investigational Site Number 032012 Santa Fe
Argentina Investigational Site Number 032009 Tucumán
Australia Investigational Site Number 036004 Adelaide
Australia Investigational Site Number 036002 Brisbane
Australia Investigational Site Number 036005 Campbelltown
Australia Investigational Site Number 036001 Clayton
Australia Investigational Site Number 036008 Frankston
Australia Investigational Site Number 036003 Nedlands
Australia Investigational Site Number 036009 Prahran
Australia Investigational Site Number 036006 Woolloongabba
Chile Investigational Site Number 152007 Quillota
Chile Investigational Site Number 152001 Santiago
Chile Investigational Site Number 152002 Santiago
Chile Investigational Site Number 152003 Santiago
Chile Investigational Site Number 152005 Santiago
Chile Investigational Site Number 152011 Santiago
Chile Investigational Site Number 152012 Santiago
Chile Investigational Site Number 152013 Santiago
Chile Investigational Site Number 152014 Santiago
Chile Investigational Site Number 152008 Talca
Chile Investigational Site Number 152006 Viña Del Mar
France Investigational Site Number 250009 Brest Cedex
France Investigational Site Number 250004 Grenoble Cedex 09
France Investigational Site Number 250010 Lille
France Investigational Site Number 250006 Lyon
France Investigational Site Number 250001 Marseille
France Investigational Site Number 250002 Montpellier
France Investigational Site Number 250005 Nantes
France Investigational Site Number 250007 Nimes
France Investigational Site Number 250003 Pessac
France Investigational Site Number 250008 Strasbourg
France Investigational Site Number 250011 Vernon
Italy Investigational Site Number 380010 Ancona
Italy Investigational Site Number 380009 Catania
Italy Investigational Site Number 380004 Ferrara
Italy Investigational Site Number 380002 Firenze
Italy Investigational Site Number 380008 Foggia
Italy Investigational Site Number 380003 Modena
Italy Investigational Site Number 380007 Padova
Italy Investigational Site Number 380001 Pisa
Italy Investigational Site Number 380005 Torino
Italy Investigational Site Number 380006 Verona
Japan Investigational Site Number 392009 Asahi-Shi
Japan Investigational Site Number 392037 Chiyoda-Ku
Japan Investigational Site Number 392002 Chuo-Ku
Japan Investigational Site Number 392007 Chuoh-Ku
Japan Investigational Site Number 392012 Edogawa-Ku
Japan Investigational Site Number 392017 Fukuoka-Shi
Japan Investigational Site Number 392021 Fukuyama-Shi
Japan Investigational Site Number 392030 Habikino-Shi
Japan Investigational Site Number 392004 Himeji-Shi
Japan Investigational Site Number 392032 Hirakata-Shi
Japan Investigational Site Number 392013 Iizuka-Shi
Japan Investigational Site Number 392042 Isesaki-Shi
Japan Investigational Site Number 392026 Itabashi-Ku
Japan Investigational Site Number 392023 Kanazawa-Shi
Japan Investigational Site Number 392001 Kitakyushu-Shi
Japan Investigational Site Number 392022 Kiyose-Shi
Japan Investigational Site Number 392025 Kobe-Shi
Japan Investigational Site Number 392040 Kodaira-Shi
Japan Investigational Site Number 392044 Kokubunji-Shi
Japan Investigational Site Number 392010 Kurashiki-Shi
Japan Investigational Site Number 392036 Kyoto-Shi
Japan Investigational Site Number 392041 Nagaoka-Shi
Japan Investigational Site Number 392020 Naka-Gun
Japan Investigational Site Number 392015 Nakano-Ku
Japan Investigational Site Number 392005 Naruto-Shi
Japan Investigational Site Number 392043 Ohta-Shi
Japan Investigational Site Number 392019 Sagamihara-Shi
Japan Investigational Site Number 392024 Sakai-Shi
Japan Investigational Site Number 392011 Sakaide-Shi
Japan Investigational Site Number 392008 Sapporo-Shi
Japan Investigational Site Number 392034 Sapporo-Shi
Japan Investigational Site Number 392038 Setagaya-Ku
Japan Investigational Site Number 392028 Sumida-Ku
Japan Investigational Site Number 392006 Tomakomai-Shi
Japan Investigational Site Number 392003 Toride-Shi
Japan Investigational Site Number 392029 Tsu-Shi
Japan Investigational Site Number 392018 Tsukubo-Gun
Japan Investigational Site Number 392045 Uruma-Shi
Japan Investigational Site Number 392014 Yokohama-Shi
Japan Investigational Site Number 392035 Yokohama-Shi
Korea, Republic of Investigational Site Number 410002 Bucheon
Korea, Republic of Investigational Site Number 410003 Cheongju
Korea, Republic of Investigational Site Number 410004 Seoul
Korea, Republic of Investigational Site Number 410005 Seoul
Korea, Republic of Investigational Site Number 410001 Suwon
Mexico Investigational Site Number 484006 Chihuahua
Mexico Investigational Site Number 484005 Distrito Federal
Mexico Investigational Site Number 484001 Guadalajara
Mexico Investigational Site Number 484004 Mexico City
Mexico Investigational Site Number 484003 Monterrey
New Zealand Investigational Site Number 554001 Dunedin
New Zealand Investigational Site Number 554002 Wellington
Poland Investigational Site Number 616006 Bialystok
Poland Investigational Site Number 616003 Gdansk
Poland Investigational Site Number 616004 Gdansk
Poland Investigational Site Number 616007 Krakow
Poland Investigational Site Number 616001 Lodz
Poland Investigational Site Number 616005 Lodz
Poland Investigational Site Number 616008 Warszawa
Russian Federation Investigational Site Number 643001 Moscow
Russian Federation Investigational Site Number 643002 Moscow
Russian Federation Investigational Site Number 643003 Moscow
Russian Federation Investigational Site Number 643007 Moscow
Russian Federation Investigational Site Number 643012 Moscow
Russian Federation Investigational Site Number 643006 Novosibirsk
Russian Federation Investigational Site Number 643010 Saint-Petersburg
Russian Federation Investigational Site Number 643011 Saint-Petersburg
Russian Federation Investigational Site Number 643009 St-Petersburg
Russian Federation Investigational Site Number 643008 Yaroslavl
South Africa Investigational Site Number 710001 Cape Town
South Africa Investigational Site Number 710002 Cape Town
Spain Investigational Site Number 724001 Barcelona
Spain Investigational Site Number 724002 Barcelona
Spain Investigational Site Number 724005 Barcelona
Spain Investigational Site Number 724004 Cáceres
Spain Investigational Site Number 724006 Pozuelo De Alarcón
Spain Investigational Site Number 724003 Sabadell
Spain Investigational Site Number 724007 Sant Boi De Llobregat
Turkey Investigational Site Number 792011 Amasya
Turkey Investigational Site Number 792002 Ankara
Turkey Investigational Site Number 792008 Bursa
Turkey Investigational Site Number 792001 Istanbul
Turkey Investigational Site Number 792003 Istanbul
Turkey Investigational Site Number 792004 Istanbul
Turkey Investigational Site Number 792007 Istanbul
Turkey Investigational Site Number 792005 Izmir
Turkey Investigational Site Number 792013 Kirikkale
Turkey Investigational Site Number 792006 Mersin
Ukraine Investigational Site Number 804016 Donetsk
Ukraine Investigational Site Number 804001 Kharkiv
Ukraine Investigational Site Number 804003 Kyiv
Ukraine Investigational Site Number 804004 Kyiv
Ukraine Investigational Site Number 804008 Kyiv
Ukraine Investigational Site Number 804018 Kyiv
Ukraine Investigational Site Number 804020 Kyiv
Ukraine Investigational Site Number 804006 Odessa
Ukraine Investigational Site Number 804002 Poltava
Ukraine Investigational Site Number 804019 Vinnytsya
Ukraine Investigational Site Number 804015 Yalta
Ukraine Investigational Site Number 804012 Zaporozhye
United States Investigational Site Number 840048 Albany Georgia
United States Investigational Site Number 840028 Baltimore Maryland
United States Investigational Site Number 840015 Cincinnati Ohio
United States Investigational Site Number 840020 Cincinnati Ohio
United States Investigational Site Number 840025 Cincinnati Ohio
United States Investigational Site Number 840032 Colorado Springs Colorado
United States Investigational Site Number 840040 Colorado Springs Colorado
United States Investigational Site Number 840023 Dallas Texas
United States Investigational Site Number 840027 Daytona Beach Florida
United States Investigational Site Number 840006 Denver Colorado
United States Investigational Site Number 840024 Denver Colorado
United States Investigational Site Number 840043 Denver Colorado
United States Investigational Site Number 840005 El Paso Texas
United States Investigational Site Number 840053 Evansville Indiana
United States Investigational Site Number 840054 Everett Washington
United States Investigational Site Number 840050 Fullerton California
United States Investigational Site Number 840041 Huntington Beach California
United States Investigational Site Number 840031 Lake Oswego Oregon
United States Investigational Site Number 840019 Los Angeles California
United States Investigational Site Number 840022 Los Angeles California
United States Investigational Site Number 840029 Los Angeles California
United States Investigational Site Number 840017 Louisville Kentucky
United States Investigational Site Number 840034 Medford Oregon
United States Investigational Site Number 840039 Miami Florida
United States Investigational Site Number 840018 Minneapolis Minnesota
United States Investigational Site Number 840013 Mission Viejo California
United States Investigational Site Number 840037 Missoula Montana
United States Investigational Site Number 840044 Newport Beach California
United States Investigational Site Number 840045 North Dartmouth Massachusetts
United States Investigational Site Number 840046 Novi Michigan
United States Investigational Site Number 840051 Novi Michigan
United States Investigational Site Number 840001 Oklahoma City Oklahoma
United States Investigational Site Number 840030 Owensboro Kentucky
United States Investigational Site Number 840004 Papillion Nebraska
United States Investigational Site Number 840042 Philadelphia Pennsylvania
United States Investigational Site Number 840010 Pittsburgh Pennsylvania
United States Investigational Site Number 840011 Princeton New Jersey
United States Investigational Site Number 840035 Richmond Virginia
United States Investigational Site Number 840026 River Forest Illinois
United States Investigational Site Number 840007 Riverside California
United States Investigational Site Number 840016 Rochester New York
United States Investigational Site Number 840014 Rolling Hills Estates California
United States Investigational Site Number 840008 San Antonio Texas
United States Investigational Site Number 840036 San Jose California
United States Investigational Site Number 840021 Spartanburg South Carolina
United States Investigational Site Number 840002 St Louis Missouri
United States Investigational Site Number 840003 St Louis Missouri
United States Investigational Site Number 840033 Tacoma Washington
United States Investigational Site Number 840009 Upland Pennsylvania
United States Investigational Site Number 840052 Wheaton Maryland

Sponsors (2)

Lead Sponsor Collaborator
Sanofi Regeneron Pharmaceuticals

Countries where clinical trial is conducted

United States,  Argentina,  Australia,  Chile,  France,  Italy,  Japan,  Korea, Republic of,  Mexico,  New Zealand,  Poland,  Russian Federation,  South Africa,  Spain,  Turkey,  Ukraine, 

Outcome

Type Measure Description Time frame Safety issue
Primary Change from baseline in forced expiratory volume (FEV1) Week 12 No
Secondary Relative change from baseline in FEV1 Week 12 No
Secondary Annualized rate of loss of asthma control Week 24 No
Secondary Time to loss of asthma control Week 24 No
Secondary Change from baseline in asthma symptom scores Week 12 No
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