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An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy — TOPAZ  

Spinal Muscular Atrophy Clinical Trial

Official title:
Phase 2 Active Treatment Study to Evaluate the Efficacy and Safety of SRK-015 in Patients With Later-Onset Spinal Muscular Atrophy (TOPAZ)

Clinical Trial Summary

The TOPAZ study will assess the safety and efficacy of SRK-015 in later-onset Spinal Muscular Atrophy (SMA Type 2 and Type 3) in pediatric and adult patients.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT03921528
Study type Interventional
Source Scholar Rock, Inc.
Contact
Status Completed
Phase Phase 2
Start date April 22, 2019
Completion date February 28, 2024
View Details
See also
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