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NCT00713453 Clinical Trial

Muscle Response to Enzyme Replacement Therapy in Pompe Disease

Pompe Disease Clinical Trial

Official title:
Muscle Response to Enzyme Replacement Therapy in Pompe Disease

Clinical Trial Details — Status: Recruiting

Administrative data
NCT number NCT00713453
Other study ID # 200704066R
Secondary ID
Status Recruiting
Phase N/A
First received July 9, 2008
Last updated March 21, 2015
Start date January 2007
Est. completion date December 2019

Study information
Verified date March 2015
Source National Taiwan University Hospital
Contact Yin-Hsiu Chien, MD
Phone 886-2-23123456
Email chienyh@ntu.edu.tw
Is FDA regulated No
Health authority Taiwan: Department of Health
Study type Observational

Clinical Trial Summary

This study is to study the response of muscle cells from Pompe disease after enzyme replacement therapy

Recruitment information / eligibility
Status Recruiting
Enrollment 16
Est. completion date December 2019
Est. primary completion date December 2019
Accepts healthy volunteers Accepts Healthy Volunteers
Gender Both
Age group N/A and older
Eligibility Inclusion Criteria:

- patients with Pompe disease, prepare or on enzyme replacement therapy

- signed informed consent

Exclusion Criteria:

Study Design

Observational Model: Case-Only

Related Conditions & MeSH terms

Locations
Country Name City State
Taiwan National Taiwan University Hospital Taipei

Sponsors (1)
Lead Sponsor Collaborator
National Taiwan University Hospital

Country where clinical trial is conducted

Taiwan, 

Outcome
Type Measure Description Time frame Safety issue
Primary all morphology changes improvement 6 months Yes
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